Found 6 matching trials
Safety and Exercise Study of Two Doses of BMN 110 for Morquio A Syndrome
PHASE2The primary objective of this study was to evaluate the safety of a 2.0 mg/...
Location
Multiple Locations
Efficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation
PHASE2The primary objective of this study is to evaluate the effect of 2.0 mg/kg/...
Location
Children's Hospital & Research Center Oakland
Long-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)
PHASE3This Phase 3 extension study will evaluate the long-term efficacy and safet...
Location
Multiple Locations
Study of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome)
PHASE2This open-label Phase 2 study will evaluate the safety and efficacy of week...
Location
Multiple Locations
A Study to Evaluate the Safety, Tolerability and Efficacy of BMN 110 in Subjects With Mucopolysaccharidosis IVA
PHASE1This multicenter, open-label study is designed to assess safety, dose-respo...
Location
Multiple Locations
A Double-Blind Study to Evaluate the Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)
PHASE3This Phase 3 study will evaluate the efficacy and safety of 2.0 mg/kg/week ...
Location
Multiple Locations